Other terms
- Genitourinary System
- Genomics
- Geriatric Neurology
- Glaucoma
- Good Clinical Practice (GCP)
- Good Laboratory Practices (GLP)
- Gynecology
- Hair Follicle
- Health Insurance Portability and Accountability Act (HIPAA) Privacy Rule
- Healthy volunteers
- Heart Failure (HF)
- Helical Computed Tomography (Helical CT)
Gene Therapy
What is Gene Therapy? Gene therapy is a medical approach that aims to treat or prevent disease via gene modification. This therapy involves introducing, inactivating, or replacing specific genes to target conditions such as cancer, genetic disorders, and infectious diseases.
Types of Gene Therapy
Plasmid DNA
Plasmid DNA introduces therapeutic genes into human cells using genetically engineered circular DNA molecules.
Viral vectors
Researchers use genetically modified viruses as vectors to carry therapeutic genes into human cells after removing their ability to cause infectious diseases.
Bacterial vectors
Researchers can modify bacteria to prevent them from causing infectious diseases and utilize them as vectors (vehicles) to carry therapeutic genes into human tissues.
Human gene editing technology
Techniques such as CRISPR-Cas9 enable precise modifications to DNA, allowing for the correction of genetic defects or the introduction of desired genetic characteristics.
Patient-derived cellular gene therapy products
Patient-derived cellular gene therapy products involve the modification of a patient’s own cells to treat or potentially cure diseases at the genetic level. In this therapy, cells are extracted from the patient, genetically modified, and then reintroduced into the patient.