Molecule Structure

Scientific Name

Risdiplam

Description of the Drug

Risdiplam is an oral mRNA splicing modifier used in the treatment of spinal muscular atrophy (SMA).

Source: DrugBank Online – DrugBank.com. Retrieved 2023-03-10 from
http://www.drugbank.ca/drugs/DB15305

Brand Name(s)

Evrysdi

Company Owner(s)

Genentech Inc

Mechanism(s) Of Action

Target Name Target Type Action Type Target ChEMBL ID
SMN2 pre-mRNA NUCLEIC-ACID POSITIVE MODULATOR CHEMBL3826841

Unichem Links

SureChEMBL SCHEMBL17260852
Human Metabolome Database HMDB0304853
DrugBank DB15305
PubChem 118513932
DrugCentral 5407
ChemicalBook CB64674494
Guide to Pharmacology 11170
rxnorm RISDIPLAM